- ongoing, recruitingTherapeutic confirmatory (Phase III)
A Multi-center, Randomized, Double-blind, Placebo-controlled Trial to Evaluate the Neurological Effects of EryDex on subjects with Ataxia-Telangiectasia.
This study is looking for children and adults with Ataxia-Telangiectasia (A-T) to see if a new treatment called EryDex can help with their symptoms. It compares EryDex to a dummy treatment (placebo) to find out if it's effective and safe.
Poland · Norway · Denmark - active not recruitingPHASE3
A Pivotal Study of N-Acetyl-L-Leucine on Ataxia-Telangiectasia (A-T)
This study is testing a new medicine, N-Acetyl-L-Leucine, for Ataxia-Telangiectasia (A-T). It aims to see if the medicine is safe, well-tolerated, and effective in improving symptoms, compared to a dummy treatment.
United States · Germany · Slovakia