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Retinitis Pigmentosa (RP) research hub

2 indexed studies · 0 currently recruiting

active not recruitingPHASE2
Study to Evaluate Ultevursen in Subjects With Retinitis Pigmentosa (RP) Due to Mutations in Exon 13 of the USH2A Gene
This study is looking at a new treatment called Ultevursen for a type of eye problem called Retinitis Pigmentosa (RP) caused by specific gene changes. It's in the second stage of testing, focusing on how safe and well people tolerate the treatment when it's given as an injection into the eye.
United States · Belgium · Brazil
active not recruitingPHASE2, PHASE3
A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE)
This study looks at a new treatment called sepofarsen for a rare eye condition called Leber Congenital Amaurosis 10 (LCA10), which causes blindness. We want to see if it helps improve sight, how safe it is, and how well people tolerate it.
United States · Belgium · Brazil